RARE

Ultragenyx Pharmaceutical Inc.

Nasdaq · Pharmaceutical Preparations · Inc. DE · CIK 0001515673
$21.59 -1.46% $2.1B
Insider Selling Cluster (2 insiders)High Impact Filing (8/10)6 New Institutional Positions
Vol
Market Cap$2.1B
Cap SizeMid Cap
Inst. Holders9 funds
Inst. Value$429.7M
Inst. Activity6 buys / 1 sells
Insider Activity0B / 14S
Insider Net $-$2.9M
Reddit Sentiment50° Neutral
SEC Reports5
Exchange Nasdaq·Sector Pharmaceutical Preparations·Inc. DE·CIK 0001515673·Prev Close $21.91

Recent Activity

Sep 19, 2026 fda_pdufa
PDUFA: RARE — UX111 in Sanfilippo syndrome type A (MPS IIIA) — 2026-09-19
FDA target action date 2026-09-19 for RARE (Ultragenyx Pharmaceutical Inc.). Drug: UX111. Indication
Jun 1, 2026 Insider
Horn Howard sold 4,653 shares
Chief Financial Officer @ $23.77 ($110.6K)
May 18, 2026 Insider
SULIMAN SHEHNAAZ sold 5,740 shares
Director @ $25.12 ($144.2K)
May 14, 2026 Insider
Dunsire Deborah sold 7,751 shares
Director @ $0.00 ($0.00)
May 6, 2026 SEC
Two Ultragenyx insiders (CFO and Chief Medical Officer) sold a combined $125K in open-market transactions over the past
CLUSTER — Impact 2/10
May 5, 2026 SEC
Ultragenyx reported Q1 2026 revenue of $136M (consensus $158.4M) and EPS of -$1.84 (consensus -$1.46), both missing expe
PRESS-RELEASE — Impact 6/10
Apr 2, 2026 SEC
Ultragenyx Pharmaceutical Inc. announced that the FDA has accepted for review its resubmitted Biologics License Applicat
8-K — Impact 8/10
Inst.
FMR LLC — TRIM
2,666,249 shares ($61.3M)

Price Targets

Historical data — last covering-analyst action Oct 2024. No current recommendation available.
$52.05 (Oct 2024)
Current $22.79 Low $25.00 Median $48.00 High $96.00 19 analysts
$25.00 $96.00

Analyst Ratings

Historical distribution88% buy · 25 analysts · last covering-analyst action Oct 2024
8Strong Buy
14Buy
3Hold
0Sell
0Strong Sell
Historical Analyst Actions
DateFirmActionRating
Oct 22, 2024 Cantor Fitzgerald REITERATE Overweight → Overweight
Oct 21, 2024 TD Cowen MAINTAIN Buy → Buy
Oct 1, 2024 Cantor Fitzgerald REITERATE Overweight → Overweight
Sep 26, 2024 RBC Capital REITERATE Outperform → Outperform
Sep 20, 2024 Cantor Fitzgerald REITERATE Overweight → Overweight

Earnings Estimates

PeriodEPS Est.RangeGrowth#
Current Q $-1.14 ▼ -0.6% $-1.46 — $-0.78 2% YoY 4
Next Q $-0.95 ▲ +6.7% $-1.38 — $-0.63 48% YoY 3
Current FY $-4.24 ▲ +5.0% $-4.41 — $-4.12 27% YoY 4
Next FY $0.97 ▲ +7682.5% $-1.60 — $5.61 123% YoY 4

Top Institutional Holders

FundValueMove
VANGUARD GROUP INC$236.1M
FMR LLC$61.3MTRIM
MORGAN STANLEY$42.0MDOUBLED
NORGES BANK$29.0MNEW
BANK OF AMERICA CORP$27.9MADD

Recent Insider Trades

DateInsiderTypeValue
Jun 1, 2026Horn HowardSELL$110.6K
May 18, 2026SULIMAN SHEHNAAZSELL$144.2K
May 14, 2026Dunsire DeborahA$0.00
May 14, 2026Dunsire DeborahA$0.00
May 14, 2026WELCH DANIELA$0.00

Reddit Sentiment

50°
Neutral
Bearish Neutral Bullish
2 mentions 0 bullish 0 bearish
9 institutional holders with $429.7M total value (18,683,949 shares) as of 2025-Q4. Top holders: VANGUARD, FMR, MORGAN. Net buying activity: 6 institutions added/increased vs 1 reduced.

Top Institutional Holders — 2025-Q4

#FundSharesValue% of TrackedLast Move
1VANGUARD GROUP INC10,263,815$236.1M54.9%
2FMR LLC2,666,249$61.3M14.3%TRIM -63.4%
3MORGAN STANLEY1,826,295$42.0M9.8%DOUBLED +100.7%
4NORGES BANK1,261,026$29.0M6.7%NEW
5BANK OF AMERICA CORP /DE/1,213,928$27.9M6.5%ADD +85.3%
6CHARLES SCHWAB INVESTMENT MANAGEMENT INC598,924$13.8M3.2%NEW
7TWO SIGMA INVESTMENTS, LP424,049$9.8M2.3%ADD +30.0%
8RENAISSANCE TECHNOLOGIES LLC366,100$8.4M2.0%DOUBLED +1571.7%
9WELLS FARGO & COMPANY/MN63,563$1.5M0.3%DOUBLED +154.8%

Recent Position Changes

FundActionPrev SharesCurr SharesChange %ValueQuarter
FMR LLCTRIM7,283,2962,666,249-63.4%$61.3M2025-Q4
MORGAN STANLEYDOUBLED910,1831,826,295+100.7%$42.0M2025-Q4
NORGES BANKNEW1,261,026$29.0M2025-Q4
BANK OF AMERICA CORP /DE/ADD655,0211,213,928+85.3%$27.9M2025-Q4
TWO SIGMA INVESTMENTS, LPADD326,180424,049+30.0%$9.8M2025-Q4
RENAISSANCE TECHNOLOGIES LLCDOUBLED21,900366,100+1571.7%$8.4M2025-Q4
WELLS FARGO & COMPANY/MNDOUBLED24,94863,563+154.8%$1.5M2025-Q4
FMR LLCDOUBLED2,604,5887,283,296+179.6%$219.1M2025-Q3
MORGAN STANLEYADD638,879910,183+42.5%$27.4M2025-Q3
TWO SIGMA INVESTMENTS, LPTRIM576,901326,180-43.5%$9.8M2025-Q3
WELLS FARGO & COMPANY/MNADD17,44024,948+43.1%$750.4K2025-Q3
RENAISSANCE TECHNOLOGIES LLCNEAR_EXIT208,30021,900-89.5%$658.8K2025-Q3
NORGES BANKEXIT983,6380-100.0%$0.002025-Q3
FMR LLCDOUBLED381,4222,604,588+582.9%$94.7M2025-Q2
NORGES BANKNEW983,638$35.8M2025-Q2
BANK OF AMERICA CORP /DE/ADD527,980672,390+27.4%$24.4M2025-Q2
RENAISSANCE TECHNOLOGIES LLCTRIM299,600208,300-30.5%$7.6M2025-Q2
UBS Group AGADD325,651469,482+44.2%$17.0M2025-Q1
WELLS FARGO & COMPANY/MNTRIM30,37117,269-43.1%$625.3K2025-Q1
NORGES BANKEXIT961,7940-100.0%$0.002025-Q1
MORGAN STANLEYADD467,836598,189+27.9%$25.2M2024-Q4
CITADEL ADVISORS LLCDOUBLED105,253374,979+256.3%$15.8M2024-Q4
UBS Group AGDOUBLED93,069325,651+249.9%$13.7M2024-Q4
RENAISSANCE TECHNOLOGIES LLCADD182,100254,700+39.9%$10.7M2024-Q4
CHARLES SCHWAB INVESTMENT MANAGEMENT INCNEW594,521$33.0M2024-Q3
15 unique insiders with 14 transactions. Net insider value: -$2.9M ($0.00 bought, $2.9M sold).

Insider Transactions

DateInsiderTitleTypeSharesPriceValue
Jun 1, 2026Horn HowardChief Financial OfficerSELL4,653$23.77$110.6K
May 18, 2026SULIMAN SHEHNAAZDirectorSELL5,740$25.12$144.2K
May 14, 2026Dunsire DeborahDirectorA7,751$0.00$0.00
May 14, 2026Dunsire DeborahDirectorA14,058$0.00$0.00
May 14, 2026WELCH DANIEL GDirectorA7,751$0.00$0.00
May 14, 2026WELCH DANIEL GDirectorA14,058$0.00$0.00
May 14, 2026NARACHI MICHAELDirectorA7,751$0.00$0.00
May 14, 2026NARACHI MICHAELDirectorA14,058$0.00$0.00
May 14, 2026Sanders Corazon (Corsee) D.DirectorA7,751$0.00$0.00
May 14, 2026Sanders Corazon (Corsee) D.DirectorA14,058$0.00$0.00
May 14, 2026Ray AmritDirectorA7,751$0.00$0.00
May 14, 2026Ray AmritDirectorA14,058$0.00$0.00
May 14, 2026SULIMAN SHEHNAAZDirectorA7,751$0.00$0.00
May 14, 2026SULIMAN SHEHNAAZDirectorA14,058$0.00$0.00
May 14, 2026Fust Matthew KDirectorA7,751$0.00$0.00
May 14, 2026Fust Matthew KDirectorA14,058$0.00$0.00
May 5, 2026Crombez EricEVP and Chief Medical OfficerSELL344$24.96$8.6K
May 1, 2026Horn HowardChief Financial OfficerSELL4,683$24.90$116.6K
Apr 22, 2026Huizenga Theodore AlanSVP, Chief Accounting OfficerA20,241$0.00$0.00
Apr 22, 2026Huizenga Theodore AlanSVP, Chief Accounting OfficerA7,348$0.00$0.00
Apr 16, 2026Horn HowardChief Financial OfficerA34,674$0.00$0.00
Apr 16, 2026Horn HowardChief Financial OfficerA59,952$0.00$0.00
Apr 16, 2026Crombez EricEVP and Chief Medical OfficerA34,674$0.00$0.00
Apr 16, 2026Crombez EricEVP and Chief Medical OfficerA59,952$0.00$0.00
Apr 16, 2026Parschauer Karah HerdmanEVP and Chief Legal OfficerA49,960$0.00$0.00
Apr 16, 2026Harris ErikEVP & Chief Commercial OfficerA28,895$0.00$0.00
Apr 16, 2026Harris ErikEVP & Chief Commercial OfficerA49,960$0.00$0.00
Apr 16, 2026Parschauer Karah HerdmanEVP and Chief Legal OfficerA28,895$0.00$0.00
Apr 16, 2026Pinion John RichardSee RemarksA23,116$0.00$0.00
Apr 16, 2026Pinion John RichardSee RemarksA79,936$0.00$0.00
Apr 16, 2026Huang Dennis KarlSee RemarksA23,116$0.00$0.00
Apr 16, 2026Huang Dennis KarlSee RemarksA79,936$0.00$0.00
Apr 16, 2026KAKKIS EMIL DPresident & CEOA76,745$0.00$0.00
Apr 16, 2026KAKKIS EMIL DPresident & CEOA132,693$0.00$0.00
Apr 1, 2026Horn HowardChief Financial OfficerSELL4,683$20.97$98.2K
Mar 10, 2026Parschauer Karah HerdmanEVP and Chief Legal OfficerSELL3,508$22.67$79.5K
Mar 6, 2026Parschauer Karah HerdmanEVP and Chief Legal OfficerSELL6,018$21.40$128.8K
Mar 3, 2026Horn HowardChief Financial OfficerSELL1,635$22.40$36.6K
Mar 2, 2026Pinion John RichardSee RemarksSELL10,029$22.80$228.7K
Mar 2, 2026Parschauer Karah HerdmanEVP and Chief Legal OfficerSELL8,135$22.80$185.5K
Mar 2, 2026Horn HowardChief Financial OfficerSELL5,290$22.80$120.6K
Mar 2, 2026Huang Dennis KarlSee RemarksF999$23.39$23.4K
Mar 2, 2026Harris ErikEVP & Chief Commercial OfficerSELL10,539$22.80$240.3K
Mar 2, 2026Huizenga Theodore AlanSVP, Chief Accounting OfficerF148$23.39$3.5K
Mar 2, 2026Crombez EricEVP and Chief Medical OfficerSELL7,029$22.80$160.3K
Mar 2, 2026KAKKIS EMIL DPresident & CEOSELL54,404$22.80$1.2M
Mar 1, 2026Pinion John RichardSee RemarksA11,137$0.00$0.00
Mar 1, 2026Parschauer Karah HerdmanEVP and Chief Legal OfficerA11,137$0.00$0.00
Mar 1, 2026Horn HowardChief Financial OfficerA6,143$0.00$0.00
Mar 1, 2026Huang Dennis KarlSee RemarksA11,137$0.00$0.00

No press releases analyzed yet. Press releases are collected from GlobeNewsWire and analyzed by the LLM pipeline.

Historical analyst distribution (last covering-analyst action Oct 2024): 88% buy across 25 analysts — 8 strong buy, 14 buy, 3 hold, 0 sell, 0 strong sell. No current recommendation available.

Analyst Price Targets

Historical data — last covering-analyst action Oct 2024. No current recommendation available.
$52.05 mean target (Oct 2024)
$25.00 Low $96.00 High
MetricValue
Current Price$22.79
Target Low$25.00
Target Mean$52.05
Target Median$48.00
Target High$96.00
# Analysts19
Recommendation— (no recent coverage)

Earnings Estimates & Revisions

PeriodEPS AvgEPS LowEPS HighEPS Growth30d Rev.Up/DownRev. AvgRev. GrowthAnalysts
Current Q
2026-06-30
$-1.14 $-1.46 $-0.78 2.3% -0.6% 0↑ 3↓ $0.2B 9.2% 4
Next Q
2026-09-30
$-0.95 $-1.38 $-0.63 47.6% +6.7% 0↑ 3↓ $0.2B 15.0% 3
Current FY
2026-12-31
$-4.24 $-4.41 $-4.12 27.2% +5.0% 0↑ 2↓ $0.7B 10.2% 4
Next FY
2027-12-31
$0.97 $-1.60 $5.61 122.7% +7682.5% 0↑ 1↓ $1.0B 32.7% 4

Current Quarter EPS Revision History

TimepointEPS EstimateChange
Current$-1.144
7d ago$-1.222+0.078
30d ago$-1.137-0.006
60d ago$-1.129-0.014
90d ago$-1.070-0.074
17 analyst firms have rated this stock: 2 upgrades, 0 downgrades, 2 initiations.

Historical Analyst Actions

DateAnalyst FirmActionPrevious RatingNew Rating
Oct 22, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Oct 21, 2024 TD Cowen MAINTAIN Buy Buy
Oct 1, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Sep 26, 2024 RBC Capital REITERATE Outperform Outperform
Sep 20, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Sep 16, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Aug 5, 2024 Barclays MAINTAIN Overweight Overweight
Aug 2, 2024 Wells Fargo MAINTAIN Overweight Overweight
Aug 2, 2024 Goldman Sachs MAINTAIN Buy Buy
Aug 2, 2024 Cantor Fitzgerald MAINTAIN Overweight Overweight
Aug 2, 2024 Wedbush MAINTAIN Neutral Neutral
Jul 23, 2024 Canaccord Genuity MAINTAIN Buy Buy
Jul 22, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Jul 18, 2024 Wedbush REITERATE Neutral Neutral
Jun 12, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Jun 6, 2024 Goldman Sachs UPGRADE Neutral Buy
May 31, 2024 Wedbush MAINTAIN Neutral Neutral
May 31, 2024 B of A Securities MAINTAIN Buy Buy
May 31, 2024 Canaccord Genuity MAINTAIN Buy Buy
May 31, 2024 Cantor Fitzgerald MAINTAIN Overweight Overweight
May 31, 2024 Stifel MAINTAIN Buy Buy
May 31, 2024 Baird MAINTAIN Outperform Outperform
May 6, 2024 Canaccord Genuity MAINTAIN Buy Buy
May 3, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
May 3, 2024 Wedbush MAINTAIN Neutral Neutral
Apr 24, 2024 TD Cowen MAINTAIN Buy Buy
Apr 22, 2024 RBC Capital INITIATE Outperform
Apr 17, 2024 Wedbush REITERATE Neutral Neutral
Apr 16, 2024 Wedbush REITERATE Neutral Neutral
Apr 5, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Mar 18, 2024 JP Morgan MAINTAIN Overweight Overweight
Feb 27, 2024 JP Morgan MAINTAIN Overweight Overweight
Feb 27, 2024 Cantor Fitzgerald MAINTAIN Overweight Overweight
Feb 21, 2024 Canaccord Genuity MAINTAIN Buy Buy
Feb 16, 2024 Wedbush MAINTAIN Neutral Neutral
Feb 15, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Jan 30, 2024 Baird MAINTAIN Outperform Outperform
Jan 19, 2024 Cantor Fitzgerald REITERATE Overweight Overweight
Dec 8, 2023 Wells Fargo INITIATE Overweight
Nov 3, 2023 Morgan Stanley MAINTAIN Overweight Overweight
Oct 25, 2023 Piper Sandler MAINTAIN Overweight Overweight
Oct 10, 2023 Morgan Stanley MAINTAIN Overweight Overweight
Sep 25, 2023 Cantor Fitzgerald REITERATE Overweight Overweight
Aug 4, 2023 Morgan Stanley REITERATE Overweight Overweight
Aug 1, 2023 HC Wainwright & Co. REITERATE Buy Buy
Jun 7, 2023 Citigroup MAINTAIN Buy Buy
Jun 6, 2023 Evercore ISI Group UPGRADE In-Line Outperform
Jun 6, 2023 Wedbush MAINTAIN Neutral Neutral
May 8, 2023 Wedbush MAINTAIN Neutral
May 5, 2023 Citigroup MAINTAIN Buy Buy

Monthly Consensus History

PeriodStrong BuyBuyHoldSellStrong SellBuy %Distribution
Jun 1, 202681430088%
May 1, 202681530088%
Apr 1, 202681530088%
Mar 1, 202691620093%
Feb 1, 202691620093%
Jan 1, 202691620093%
Strong BuyBuyHoldSellStrong Sell

No congressional trading data available for this ticker. Data is sourced from Senate and House financial disclosure filings.

50°
Neutral
Bearish Neutral Bullish
2 mentions 0 bullish 0 bearish 2 time periods

Reddit Sentiment History

DateMentionsSentimentBullishBearishThreads
Mar 24, 2026150° Neutral001
Mar 24, 2026150° Neutral001
Sep 19, 2026
fda_pdufa
PDUFA: RARE — UX111 in Sanfilippo syndrome type A (MPS IIIA) — 2026-09-19
FDA target action date 2026-09-19 for RARE (Ultragenyx Pharmaceutical Inc.). Drug: UX111. Indication: Sanfilippo syndrome type A (MPS IIIA). PDUFA tar
Aug 23, 2026
fda_pdufa
PDUFA: RARE — DTX401 in glycogen storage disease type Ia (GSDIa) — 2026-08-23
FDA target action date 2026-08-23 for RARE (Ultragenyx Pharmaceutical Inc.). Drug: DTX401. Indication: glycogen storage disease type Ia (GSDIa). PDUFA
Jun 9, 2026
short_volume
Short Volume: RARE — 56.7% short (0.3M / 0.6M)
Short: 339,197 | Exempt: 43 | TRF Vol: 597,825 | Short Ratio: 56.7% | Off-exchange volume (dark pool + OTC)
Jun 3, 2026
other
Ultragenyx to Participate at Goldman Sachs 47th Annual Global Healthcare Conference
<p>NOVATO, Calif., June 03, 2026 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the devel
Jun 3, 2026
Clinical Trial
A Comparative Phase 2 Study Assessing the Efficacy of Triheptanoin, an Anaplerotic Therapy in Huntington's Disease
Phase Phase 2 — COMPLETED
Jun 3, 2026
short_volume
Short Volume: RARE — 64.7% short (0.4M / 0.7M)
Short: 425,949 | Exempt: 0 | TRF Vol: 657,993 | Short Ratio: 64.7% | Off-exchange volume (dark pool + OTC)
Jun 1, 2026
short_volume
Short Volume: RARE — 60.3% short (0.4M / 0.6M)
Short: 362,534 | Exempt: 0 | TRF Vol: 601,513 | Short Ratio: 60.3% | Off-exchange volume (dark pool + OTC)
May 29, 2026
short_volume
Short Volume: RARE — 69.0% short (0.4M / 0.6M)
Short: 390,643 | Exempt: 9 | TRF Vol: 566,004 | Short Ratio: 69.0% | Off-exchange volume (dark pool + OTC)
May 28, 2026
short_volume
Short Volume: RARE — 60.3% short (0.3M / 0.5M)
Short: 317,615 | Exempt: 0 | TRF Vol: 526,932 | Short Ratio: 60.3% | Off-exchange volume (dark pool + OTC)
May 22, 2026
other
Ultragenyx Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)
<p>NOVATO, Calif., May 22, 2026 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the develo
May 20, 2026
short_volume
Short Volume: RARE — 61.8% short (0.3M / 0.5M)
Short: 326,985 | Exempt: 2,526 | TRF Vol: 529,485 | Short Ratio: 61.8% | Off-exchange volume (dark pool + OTC)
May 19, 2026
short_volume
Short Volume: RARE — 66.8% short (0.4M / 0.7M)
Short: 442,832 | Exempt: 298 | TRF Vol: 663,299 | Short Ratio: 66.8% | Off-exchange volume (dark pool + OTC)
May 18, 2026
dark_pool
Dark Pool: RARE — 1.9M shares, 46,695 trades
Week starting 2026-05-18. Total ATS volume: 1,942,042 shares across 46,695 trades.
May 11, 2026
dark_pool
Dark Pool: RARE — 1.6M shares, 40,256 trades
Week starting 2026-05-11. Total ATS volume: 1,639,179 shares across 40,256 trades.
May 8, 2026
short_volume
Short Volume: RARE — 65.9% short (0.3M / 0.5M)
Short: 344,817 | Exempt: 0 | TRF Vol: 523,358 | Short Ratio: 65.9% | Off-exchange volume (dark pool + OTC)
May 7, 2026
short_volume
Short Volume: RARE — 60.9% short (0.4M / 0.7M)
Short: 399,377 | Exempt: 0 | TRF Vol: 655,801 | Short Ratio: 60.9% | Off-exchange volume (dark pool + OTC)
Apr 27, 2026
Clinical Trial
Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects With Angelman Syndrome (AS)
Phase Phase 3 — ACTIVE_NOT_RECRUITING
Apr 1, 2026
Clinical Trial
A Study of Adeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With Glycogen Storage Disease Type Ia (GSDIa)
Phase Phase 3 — COMPLETED